Journal Browser

Journal Browser

Special Issue "Gene Therapy for Neurological Disorder"

A special issue of International Journal of Molecular Sciences (ISSN 1422-0067). This special issue belongs to the section "Molecular Genetics and Genomics".

Deadline for manuscript submissions: 28 February 2022.

Special Issue Editor

Prof. Dr. Enrico Maria Surace
E-Mail Website
Guest Editor
Department of Translational Medicine, University of Naples Federico II, 80131 Naples, Italy
Interests: retina; gene therapy; adeno-associated virus (AAV) vector; transcription; transcriptional repression; zinc finger; transcription factors

Special Issue Information

Dear Colleagues,

Neurological disorders cause a higher burden than any other group of diseases urging the development of therapeutic interventions. Unprecedently, these diseases are benefiting of recent progress of genetic therapies. RNA interference, Antisense Oligonucleotides (ASO), and DNA-binding platforms for gene-editing and transcriptional regulation are enabling to intervene at genome, transcriptional, and transcript levels. Furthermore, large-scale genomic studies are currently multiplying the identification of the disease targets underlying monogenic and multifactorial neurological disorders. Finally, driven by the continuous development of the delivery systems, including engineered capsids and the delivery administration techniques, genetic therapies for neurological disorders are gaining more and more momentum.

In this regard, we invite investigators to contribute original research articles and review articles that will expand the way to tackle monogenic and multifactorial neurological disorders affecting the brain, the peripheral nervous system, including those causing chronic pain, and the sense organs such as the retina and the inner ear via genetic therapies approaches.

Prof. Dr. Enrico Maria Surace
Guest Editor

Manuscript Submission Information

Manuscripts should be submitted online at www.mdpi.com by registering and logging in to this website. Once you are registered, click here to go to the submission form. Manuscripts can be submitted until the deadline. All papers will be peer-reviewed. Accepted papers will be published continuously in the journal (as soon as accepted) and will be listed together on the special issue website. Research articles, review articles as well as short communications are invited. For planned papers, a title and short abstract (about 100 words) can be sent to the Editorial Office for announcement on this website.

Submitted manuscripts should not have been published previously, nor be under consideration for publication elsewhere (except conference proceedings papers). All manuscripts are thoroughly refereed through a single-blind peer-review process. A guide for authors and other relevant information for submission of manuscripts is available on the Instructions for Authors page. International Journal of Molecular Sciences is an international peer-reviewed open access semimonthly journal published by MDPI.

Please visit the Instructions for Authors page before submitting a manuscript. There is an Article Processing Charge (APC) for publication in this open access journal. For details about the APC please see here. Submitted papers should be well formatted and use good English. Authors may use MDPI's English editing service prior to publication or during author revisions.


Neurological disorders
Genetic therapies
Neuropathic Pain
Macular degeneration, age-related
Neurometabolic Diseases
Neuromuscular Diseases
Retinal Degeneration
Inner ear
Alzheimer's disease (AD)
Angelman’s syndrome (AS)
Attention deficit-hyperactivity disorder (ADHD)
Autism spectrum disorder (ASD)
Cornelia de Lange syndrome (CDLS)
Dravet syndrome (DRVT)
Fragile X syndrome
Friedreich ataxia (FA)
Huntington's disease (HD)
Parkinson's disease (PD)
Rett’s syndrome (RS)
Spinal muscular atrophy (SMA)
Spinocerebellar ataxia (SCA)
Tuberous sclerosis (TS)

Published Papers

This special issue is now open for submission.
Back to TopTop